One-year Treatment of Morpholino Antisense Oligomer Improves Skeletal and Cardiac Muscle Functions in Dystrophic mdx Mice

Antisense therapy has been successful to skip targeted dystrophin exon with correction of frameshift and nonsense mutations of Duchenne muscular dystrophy (DMD). Systemic production of truncated but functional dystrophin proteins has been achieved in animal models. Furthermore, phase I/II clinical t...

詳細記述

保存先:
書誌詳細
主要な著者: Wu, Bo, Xiao, Bin, Cloer, Caryn, Shaban, Mona, Sali, Arpana, Lu, Peijuan, Li, Juan, Nagaraju, Kanneboyina, Xiao, Xiao, Lu, Qi Long
フォーマット: Artigo
言語:Inglês
出版事項: Nature Publishing Group 2011
主題:
Original Article
オンライン･アクセス:https://ncbi.nlm.nih.gov/pmc/articles/PMC3048192/
https://ncbi.nlm.nih.gov/pubmed/21179007
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2010.288
タグ: タグ追加
タグなし, このレコードへの初めてのタグを付けませんか!

類似資料