Hematopoietic differentiation of induced pluripotent stem cells from patients with mucopolysaccharidosis type I (Hurler syndrome)

Mucopolysaccharidosis type I (MPS IH; Hurler syndrome) is a congenital deficiency of α-L-iduronidase, leading to lysosomal storage of glycosaminoglycans that is ultimately fatal following an insidious onset after birth. Hematopoietic cell transplantation (HCT) is a life-saving measure in MPS IH. How...

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Detalhes bibliográficos
Main Authors: Tolar, Jakub, Park, In-Hyun, Xia, Lily, Lees, Chris J., Peacock, Brandon, Webber, Beau, McElmurry, Ron T., Eide, Cindy R., Orchard, Paul J., Kyba, Michael, Osborn, Mark J., Lund, Troy C., Wagner, John E., Daley, George Q., Blazar, Bruce R.
Formato: Artigo
Idioma:Inglês
Publicado em: American Society of Hematology 2011
Assuntos:
Hematopoiesis and Stem Cells
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3035077/
https://ncbi.nlm.nih.gov/pubmed/21037085
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2010-05-287607
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