Hematopoietic differentiation of induced pluripotent stem cells from patients with mucopolysaccharidosis type I (Hurler syndrome)

Mucopolysaccharidosis type I (MPS IH; Hurler syndrome) is a congenital deficiency of α-L-iduronidase, leading to lysosomal storage of glycosaminoglycans that is ultimately fatal following an insidious onset after birth. Hematopoietic cell transplantation (HCT) is a life-saving measure in MPS IH. How...

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Dettagli Bibliografici
Autori principali: Tolar, Jakub, Park, In-Hyun, Xia, Lily, Lees, Chris J., Peacock, Brandon, Webber, Beau, McElmurry, Ron T., Eide, Cindy R., Orchard, Paul J., Kyba, Michael, Osborn, Mark J., Lund, Troy C., Wagner, John E., Daley, George Q., Blazar, Bruce R.
Natura: Artigo
Lingua:Inglês
Pubblicazione: American Society of Hematology 2011
Soggetti:
Hematopoiesis and Stem Cells
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3035077/
https://ncbi.nlm.nih.gov/pubmed/21037085
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2010-05-287607
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