A carregar...

Targeting of the CNS in MPS-IH Using a Nonviral Transferrin-α-l-iduronidase Fusion Gene Product

Mucopolysaccharidosis type I (Hurler syndrome) is caused by a deficiency of the enzyme α-l-iduronidase (IDUA), and is characterized by widespread lysosomal glycosaminoglycan (GAG) accumulation. Successful treatment of central nervous system (CNS) diseases is limited by the presence of the blood–brai...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Main Authors: Osborn, Mark J, McElmurry, Ron T, Peacock, Brandon, Tolar, Jakub, Blazar, Bruce R
Formato: Artigo
Idioma:Inglês
Publicado em: 2008
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC2574880/
https://ncbi.nlm.nih.gov/pubmed/18523448
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2008.119
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!