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Mammalian Models of Duchenne Muscular Dystrophy: Pathological Characteristics and Therapeutic Applications

Duchenne muscular dystrophy (DMD) is a devastating X-linked muscle disorder characterized by muscle wasting which is caused by mutations in the DMD gene. The DMD gene encodes the sarcolemmal protein dystrophin, and loss of dystrophin causes muscle degeneration and necrosis. Thus far, therapies for t...

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Detalhes bibliográficos
Main Authors: Nakamura, Akinori, Takeda, Shin'ichi
Formato: Artigo
Idioma:Inglês
Publicado em: Hindawi Publishing Corporation 2011
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3022202/
https://ncbi.nlm.nih.gov/pubmed/21274260
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1155/2011/184393
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