Current and Future Pharmacological Treatment Strategies in X‐Linked Adrenoleukodystrophy

Mutations in the ABCD1 gene cause the clinical spectrum of the neurometabolic disorder X‐linked adrenoleukodystrophy/adrenomyeloneuropathy (X‐ALD/AMN). Currently, the most efficient therapeutic opportunity for patients with the cerebral form of X‐ALD is hematopoietic stem cell transplantation and po...

Descrición completa

Gardado en:
Detalles Bibliográficos
Main Authors: Berger, Johannes, Pujol, Aurora, Aubourg, Patrick, Forss‐Petter, Sonja
Formato: Artigo
Idioma:Inglês
Publicado: Blackwell Publishing Ltd 2010
Assuntos:
MINI‐SYMPOSIUM: X‐Linked Adrenoleukodystrophy
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC2967711/
https://ncbi.nlm.nih.gov/pubmed/20626746
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/j.1750-3639.2010.00393.x
Tags: Engadir etiqueta
Sen Etiquetas, Sexa o primeiro en etiquetar este rexistro!

Títulos similares