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Short-Term Rescue of Neonatal Lethality in a Mouse Model of Propionic Acidemia by Gene Therapy

Propionic acidemia (PA) is a metabolic disorder that causes mental retardation and that can be fatal if untreated. PA is inherited in an autosomal recessive fashion involving mutations in PCCA or PCCB encoding the α and β subunits of propionyl-CoA carboxylase (PCC). Current treatment is based on die...

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Detalhes bibliográficos
Main Authors: Hofherr, Sean E., Senac, Julien S., Chen, Christopher Y., Palmer, Donna J., Ng, Philip, Barry, Michael A.
Formato: Artigo
Idioma:Inglês
Publicado em: Mary Ann Liebert, Inc. 2009
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC2922073/
https://ncbi.nlm.nih.gov/pubmed/19025475
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2008.158
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