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Leber Congenital Amaurosis due to RPE65 Mutations and its Treatment with Gene Therapy

Leber congenital amaurosis (LCA) is a rare hereditary retinal degeneration caused by mutations in more than a dozen genes. RPE65, one of these mutated genes, is highly expressed in the retinal pigment epithelium where it encodes the retinoid isomerase enzyme essential for the production of chromopho...

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Detalles Bibliográficos
Autor Principal: Cideciyan, Artur V.
Formato: Artigo
Idioma:Inglês
Publicado: 2010
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC2903652/
https://ncbi.nlm.nih.gov/pubmed/20399883
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.preteyeres.2010.04.002
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