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Toward Gene Therapy for Cystic Fibrosis Using a Lentivirus Pseudotyped With Sendai Virus Envelopes

Gene therapy for cystic fibrosis (CF) is making encouraging progress into clinical trials. However, further improvements in transduction efficiency are desired. To develop a novel gene transfer vector that is improved and truly effective for CF gene therapy, a simian immunodeficiency virus (SIV) was...

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Main Authors: Mitomo, Katsuyuki, Griesenbach, Uta, Inoue, Makoto, Somerton, Lucinda, Meng, Cuixiang, Akiba, Eiji, Tabata, Toshiaki, Ueda, Yasuji, Frankel, Gad M, Farley, Raymond, Singh, Charanjit, Chan, Mario, Munkonge, Felix, Brum, Andrea, Xenariou, Stefania, Escudero-Garcia, Sara, Hasegawa, Mamoru, Alton, Eric WFW
Format: Artigo
Jezik:Inglês
Izdano: Nature Publishing Group 2010
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC2889732/
https://ncbi.nlm.nih.gov/pubmed/20332767
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2010.13
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