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Recent advances in understanding and managing cystic fibrosis transmembrane conductance regulator dysfunction

Cystic fibrosis is the most common autosomal recessive genetic disease in Caucasians and has been extensively studied for many decades. The cystic fibrosis transmembrane conductance regulator gene was identified in 1989. It encodes a complex protein which has numerous cellular functions. Our underst...

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Dettagli Bibliografici
Pubblicato in:F1000Prime Rep
Autori principali: Griesenbach, Uta, Alton, Eric W.F.W.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Faculty of 1000 Ltd 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4447040/
https://ncbi.nlm.nih.gov/pubmed/26097737
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.12703/P7-64
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