Comparison of Adeno-Associated Virus Pseudotype 1, 2, and 8 Vectors Administered by Intramuscular Injection in the Treatment of Murine Phenylketonuria

Lignende værker

• Correction of Murine PKU Following AAV-mediated Intramuscular Expression of a Complete Phenylalanine Hydroxylating System
  af: Ding, Zhaobing, et al.
  Udgivet: (2008)
• Phenotypic Reversion of Fair Hair upon Gene Therapy of the Phenylketonuria Mice
  af: Thöny, Beat, et al.
  Udgivet: (2014)
• High dose sapropterin dihydrochloride therapy improves monoamine neurotransmitter turnover in murine phenylketonuria (PKU)
  af: Winn, Shelley R, et al.
  Udgivet: (2015)
• The fate of intravenously administered tetrahydrobiopterin and its implications for heterologous gene therapy of phenylketonuria
  af: Harding, Cary O., et al.
  Udgivet: (2004)
• State-of-the-art 2003 on PKU gene therapy
  af: Ding, Zhaobing, et al.
  Udgivet: (2004)