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RNA Mediated Neurodegeneration in Repeat Expansion Disorders

Most neurodegenerative disorders are thought to result primarily from the accumulation of misfolded proteins which interfere with protein homeostasis in neurons. For a subset of diseases, however, non-coding regions of RNAs assume a primary toxic gain-of-function leading to degeneration in many tiss...

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Detalles Bibliográficos
Main Authors: Todd, Peter K, Paulson, Henry L
Formato: Artigo
Idioma:Inglês
Publicado: 2010
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC2852186/
https://ncbi.nlm.nih.gov/pubmed/20373340
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ana.21948
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