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Lentiviral-mediated Genetic Correction of Hematopoietic and Mesenchymal Progenitor Cells From Fanconi Anemia Patients

Previous clinical trials based on the genetic correction of purified CD34(+) cells with γ-retroviral vectors have demonstrated clinical efficacy in different monogenic diseases, including X-linked severe combined immunodeficiency, adenosine deaminase deficient severe combined immunodeficiency and ch...

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Detalhes bibliográficos
Main Authors: Jacome, Ariana, Navarro, Susana, Río, Paula, Yañez, Rosa M, González-Murillo, Africa, Luz Lozano, M, Lamana, Maria Luisa, Sevilla, Julian, Olive, Teresa, Diaz-Heredia, Cristina, Badell, Isabel, Estella, Jesus, Madero, Luis, Guenechea, Guillermo, Casado, José, Segovia, Jose C, Bueren, Juan A
Formato: Artigo
Idioma:Inglês
Publicado em: Nature Publishing Group 2009
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC2835196/
https://ncbi.nlm.nih.gov/pubmed/19277017
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2009.26
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