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Biochemical Correction of Very Long–chain Acyl-CoA Dehydrogenase Deficiency Following Adeno-associated Virus Gene Therapy

We report the development of a gene replacement strategy for very long–chain acyl-CoA dehydrogenase (VLCAD) deficiency. VLCAD is a mitochondrial enzyme involved in fatty acid β-oxidation, a key step in energy production during times of fasting or stress. Deficiency of VLCAD classically presents as h...

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Detalhes bibliográficos
Main Authors: Merritt, J. Lawrence, Nguyen, Tien, Daniels, Jan, Matern, Dietrich, Schowalter, David B.
Formato: Artigo
Idioma:Inglês
Publicado em: Nature Publishing Group 2009
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC2835097/
https://ncbi.nlm.nih.gov/pubmed/19156135
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2008.295
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