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Mutation spectrum of homogentisic acid oxidase (HGD) in alkaptonuria

Alkaptonuria (AKU) is a rare autosomal recessive metabolic disorder, characterized by accumulation of homogentisic acid, leading to darkened urine, pigmentation of connective tissue (ochronosis), joint and spine arthritis, and destruction of cardiac valves. AKU is due to mutations in the homogentisa...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Vilboux, Thierry, Kayser, Michael, Introne, Wendy, Suwannarat, Pim, Bernardini, Isa, Fischer, Roxanne, O’Brien, Kevin, Kleta, Robert, Huizing, Marjan, Gahl, William A.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2009
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC2830005/
https://ncbi.nlm.nih.gov/pubmed/19862842
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/humu.21120
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