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Supplying Clotting Factors From Hematopoietic Stem Cell–derived Erythroid and Megakaryocytic Lineage Cells

Systemically distributed proteins such as clotting factors have been traditionally expressed from muscle or liver to achieve therapeutic, long-term expression. As long-lived cell capable of generating an abundant progeny, hematopoietic stem cells (HSCs) also merit consideration for this purpose. To...

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Autores principales: Sadelain, Michel, Chang, Alex, Lisowski, Leszek
Formato: Artigo
Lenguaje:Inglês
Publicado: Nature Publishing Group 2009
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC2814379/
https://ncbi.nlm.nih.gov/pubmed/19844194
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2009.238
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