Caricamento...

Musings on genome medicine: enzyme-replacement therapy of the lysosomal storage diseases

The lysosomal storage diseases, such as Gaucher's disease, mucopolysaccharidosis I, II and IV, Fabry's disease, and Pompe's disease, are rare inherited disorders whose symptoms result from enzyme deficiency causing lysosomal accumulation. Until effective gene-replacement therapy is de...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Autori principali: Nathan, David G, Orkin, Stuart H
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2009
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2808730/
https://ncbi.nlm.nih.gov/pubmed/20017892
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/gm114
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !