A carregar...

Musings on genome medicine: enzyme-replacement therapy of the lysosomal storage diseases

The lysosomal storage diseases, such as Gaucher's disease, mucopolysaccharidosis I, II and IV, Fabry's disease, and Pompe's disease, are rare inherited disorders whose symptoms result from enzyme deficiency causing lysosomal accumulation. Until effective gene-replacement therapy is de...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Main Authors: Nathan, David G, Orkin, Stuart H
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2009
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC2808730/
https://ncbi.nlm.nih.gov/pubmed/20017892
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/gm114
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!