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In utero transplantation of monocytic cells in cats with alpha-mannosidosis

BACKGROUND: Lysosomal storage diseases are devastating illnesses, in large part because of their neurological consequences. Since significant morbidity occurs prenatally, in utero therapy is an attractive therapeutic approach. METHODS: We studied the feasibility and efficacy of in utero (IU) injecti...

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Библиографические подробности
Главные авторы: Abkowitz, Janis L., Sabo, Kathleen M., Yang, Zhantao, Vite, Charles H., Shields, Laurence E., Haskins, Mark E.
Формат: Artigo
Язык:Inglês
Опубликовано: 2009
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC2742773/
https://ncbi.nlm.nih.gov/pubmed/19667933
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/TP.0b013e3181b0d264
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