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Weekly Enzyme Replacement Therapy May Slow Decline of Renal Function in Patients with Fabry Disease Who Are on Long-Term Biweekly Dosing

This study was performed to determine whether adult male patients with Fabry disease who demonstrate a continuing decline in renal function despite 2 to 4 yr of conventionally dosed agalsidase alfa therapy (0.2 mg/kg every other week [EOW]) show an improved slope of decline with weekly administratio...

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Hlavní autoři: Schiffmann, Raphael, Askari, Hasan, Timmons, Margaret, Robinson, Chevalia, Benko, William, Brady, Roscoe O., Ries, Markus
Médium: Artigo
Jazyk:Inglês
Vydáno: 2007
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On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC1978101/
https://ncbi.nlm.nih.gov/pubmed/17409308
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1681/ASN.2006111263
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