Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

BACKGROUND: Antisense-mediated exon skipping is currently one of the most promising therapeutic approaches for Duchenne muscular dystrophy (DMD). Using antisense oligonucleotides (AONs) targeting specific exons the DMD reading frame is restored and partially functional dystrophins are produced. Foll...

Disgrifiad llawn

Wedi'i Gadw mewn:
Manylion Llyfryddiaeth
Prif Awduron: Aartsma-Rus, Annemieke, Janson, Anneke AM, van Ommen, Gert-Jan B, van Deutekom, Judith CT
Fformat: Artigo
Iaith:Inglês
Cyhoeddwyd: BioMed Central 2007
Pynciau:
Research Article
Mynediad Ar-lein:https://ncbi.nlm.nih.gov/pmc/articles/PMC1931584/
https://ncbi.nlm.nih.gov/pubmed/17612397
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1471-2350-8-43
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