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In vivo suppressor mutations correct a murine model of hereditary tyrosinemia type I

Hereditary tyrosinemia type I and alkaptonuria are disorders of tyrosine catabolism caused by deficiency of fumarylacetoacetate hydrolase (FAH) and homogentisic acid dioxygenase (HGD), respectively. Tyrosinemia is a severe childhood disease that affects the liver and kidneys, but alkaptonuria is a m...

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Detalhes bibliográficos
Main Authors: Manning, Kara, Al-Dhalimy, Muhsen, Finegold, Milton, Grompe, Markus
Formato: Artigo
Idioma:Inglês
Publicado em: The National Academy of Sciences 1999
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC18389/
https://ncbi.nlm.nih.gov/pubmed/10518553
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