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Spinal muscular atrophy: untangling the knot?

Spinal muscular atrophy (SMA), a clinically and genetically heterogeneous group of neuromuscular diseases, is a disorder of motor neurones characterised by degeneration of spinal cord anterior horn cells and muscular atrophy.
SMA is an autosomal recessive disorder with a carrier frequency of about 1...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Biros, I., Forrest, S.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: BMJ Group 1999
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC1762953/
https://ncbi.nlm.nih.gov/pubmed/9950358
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