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Glycogenosis type II: protein and DNA analysis in five South African families from various ethnic origins.

The molecular nature of lysosomal alpha-glucosidase deficiency was studied in five South African families with glycogenosis type II. Distinct ethnic origins were represented. Two new mutant acid alpha-glucosidase alleles were discovered. In two infantile patients from a consanguineous Indian family...

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Autori principali: Van der Ploeg, A T, Hoefsloot, L H, Hoogeveen-Westerveld, M, Petersen, E M, Reuser, A J
Natura: Artigo
Lingua:Inglês
Pubblicazione: 1989
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC1715658/
https://ncbi.nlm.nih.gov/pubmed/2658562
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