Evaluation of beta-globin gene therapy constructs in single copy transgenic mice.
Effective gene therapy constructs based on retrovirus or adeno-associated virus vectors will require regulatory elements that direct expression of genes transduced at single copy. Most beta-globin constructs designed for therapy of beta-thalassemias are regulated by the 5'HS2 component of the locus...
Zapisane w:
| Wydane w: | Nucleic Acids Res |
|---|---|
| Główni autorzy: | , , , , , , |
| Format: | Artigo |
| Język: | Inglês |
| Wydane: |
Oxford University Press
1997
|
| Hasła przedmiotowe: | |
| Dostęp online: | https://ncbi.nlm.nih.govhttps://pmc.ncbi.nlm.nih.gov/articles/PMC146564/ https://ncbi.nlm.nih.govhttps://pubmed.ncbi.nlm.nih.gov/9092642/ https://ncbi.nlm.nih.govhttps://doi.org/10.1093/nar/25.6.1296 |
| Etykiety: |
Nie ma etykietki, Dołącz pierwszą etykiete!
|