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Amelioration of laminin-α2-deficient congenital muscular dystrophy by somatic gene transfer of miniagrin

Congenital muscular dystrophy (CMD) is characterized by severe muscle wasting, premature death in early childhood, and lack of effective treatment. Most of the CMD cases are caused by genetic mutations of laminin-α2, which is essential for the structural integrity of muscle extracellular matrix. Her...

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Detalhes bibliográficos
Main Authors: Qiao, Chunping, Li, Jianbin, Zhu, Tong, Draviam, Romesh, Watkins, Simon, Ye, Xiaojing, Chen, Chunlian, Li, Juan, Xiao, Xiao
Formato: Artigo
Idioma:Inglês
Publicado em: National Academy of Sciences 2005
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC1189311/
https://ncbi.nlm.nih.gov/pubmed/16103356
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.0502137102
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