Treatment of the mouse model of mucopolysaccharidosis type IIIB with lentiviral-NAGLU vector

The Sanfilippo syndrome type B (mucopolysaccharidosis IIIB) is an autosomal recessive disorder due to mutations in the gene encoding NAGLU (α-N-acetylglucosaminidase), one of the enzymes required for the degradation of the GAG (glycosaminoglycan) heparan sulphate. No therapy exists for affected pati...

Descripció completa

Guardat en:
Dades bibliogràfiques
Autors principals: Di Natale, Paola, Di Domenico, Carmela, Gargiulo, Nadia, Castaldo, Sigismondo, Reyero, Enrico Gonzalez Y, Mithbaokar, Pratibha, De Felice, Mario, Follenzi, Antonia, Naldini, Luigi, Villani, Guglielmo R. D.
Format: Artigo
Idioma:Inglês
Publicat: Portland Press Ltd. 2005
Matèries:
Research Article
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC1138972/
https://ncbi.nlm.nih.gov/pubmed/15649123
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1042/BJ20041702
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!

Ítems similars