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Modeling Lysosomal Storage Diseases in the Zebrafish
Lysosomal storage diseases (LSDs) are a family of 70 metabolic disorders characterized by mutations in lysosomal proteins that lead to storage material accumulation, multiple-organ pathologies that often involve neurodegeneration, and early mortality in a significant number of patients. Along with t...
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Autores principales: | , |
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Formato: | Artigo |
Lenguaje: | Inglês |
Publicado: |
Frontiers Media S.A.
2020-05-01
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Colección: | Frontiers in Molecular Biosciences |
Materias: | |
Acceso en línea: | https://www.frontiersin.org/article/10.3389/fmolb.2020.00082/full |
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