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Organoid Technology and Its Role for Theratyping Applications in Cystic Fibrosis

Cystic fibrosis (CF) is a autosomal recessive, multisystemic disease caused by different mutations in the CFTR gene encoding CF transmembrane conductance regulator. Although symptom management is important to avoid complications, the approval of CFTR modulator drugs in the clinic has demonstrated si...

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Autores principales: Jessica Conti, Claudio Sorio, Paola Melotti
Formato: Artigo
Lenguaje:Inglês
Publicado: MDPI AG 2022-12-01
Colección:Children
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Acceso en línea:https://www.mdpi.com/2227-9067/10/1/4
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