Organoid Technology and Its Role for Theratyping Applications in Cystic Fibrosis
Cystic fibrosis (CF) is a autosomal recessive, multisystemic disease caused by different mutations in the CFTR gene encoding CF transmembrane conductance regulator. Although symptom management is important to avoid complications, the approval of CFTR modulator drugs in the clinic has demonstrated si...
Guardado en:
| Autores principales: | , , |
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| Formato: | Artigo |
| Lenguaje: | Inglês |
| Publicado: |
MDPI AG
2022-12-01
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| Colección: | Children |
| Materias: | |
| Acceso en línea: | https://www.mdpi.com/2227-9067/10/1/4 |
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