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Organoid Technology and Its Role for Theratyping Applications in Cystic Fibrosis

Cystic fibrosis (CF) is a autosomal recessive, multisystemic disease caused by different mutations in the CFTR gene encoding CF transmembrane conductance regulator. Although symptom management is important to avoid complications, the approval of CFTR modulator drugs in the clinic has demonstrated si...

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Autors principals: Jessica Conti, Claudio Sorio, Paola Melotti
Format: Artigo
Idioma:Inglês
Publicat: MDPI AG 2022-12-01
Col·lecció:Children
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Accés en línia:https://www.mdpi.com/2227-9067/10/1/4
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