Código QR (código de barras bidimensional)

EFFICACY AND SAFETY OF ENZYME REPLACEMENT THERAPY IN CHILDREN WITH MUCOPOLYSACCHARIDOSIS TYPE I, II, AND VI: A SINGLE-CENTER COHORT STUDY

Background. There are limited data on the efficacy of long-term enzyme replacement therapy (ERT) in children with mucopolysaccharidosis (MPS).Objective. Our aim was to study the efficacy and safety of long-term ERT in children with MPS type I, II, and VI.Methods. We analyzed the results of ERT with...

תיאור מלא

שמור ב:
מידע ביבליוגרפי
Principais autores: Liliia A. Osipova, Ludmila M. Kuzenkova, Leyla S. Namazova-Baranova, Anait K. Gevorkyan, Tatiana V. Podkletnova, Nikolay A. Mayanskiy, Grigoriy V. Revunenkov, Nato D. Vashakmadze
פורמט: Artigo
שפה:Inglês
יצא לאור: "Paediatrician" Publishers LLC 2018-04-01
סדרה:Вопросы современной педиатрии
נושאים:
גישה מקוונת:https://vsp.spr-journal.ru/jour/article/view/1868
תגים: הוספת תג
אין תגיות, היה/י הראשונ/ה לתייג את הרשומה!