Adeno-associated virus for cystic fibrosis gene therapy
Gene therapy is an alternative treatment for genetic lung disease, especially monogenic disorders such as cystic fibrosis. Cystic fibrosis is a severe autosomal recessive disease affecting one in 2500 live births in the white population, caused by mutation of the cystic fibrosis transmembrane conduc...
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| Autors principals: | , , |
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| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Associação Brasileira de Divulgação Científica
2011-11-01
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| Col·lecció: | Brazilian Journal of Medical and Biological Research |
| Matèries: | |
| Accés en línia: | http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0100-879X2011001100004 |
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