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Adeno-associated virus for cystic fibrosis gene therapy

Gene therapy is an alternative treatment for genetic lung disease, especially monogenic disorders such as cystic fibrosis. Cystic fibrosis is a severe autosomal recessive disease affecting one in 2500 live births in the white population, caused by mutation of the cystic fibrosis transmembrane conduc...

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Hlavní autoři: S.V. Martini, P.R.M. Rocco, M.M. Morales
Médium: Artigo
Jazyk:Inglês
Vydáno: Associação Brasileira de Divulgação Científica 2011-11-01
Edice:Brazilian Journal of Medical and Biological Research
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On-line přístup:http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0100-879X2011001100004
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