Stem/progenitor cell-based therapy for Duchenne muscular dystrophy
Duchenne muscular dystrophy is a genetic disease where loss of sarcolemma-associated protein, dystrophin, leads to progressive muscle wasting, and eventual loss of life from complications linked to cardiac deficits. Currently, numerous molecular therapies to restore dystrophin have entered clinical...
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| Autors principals: | , , |
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| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Frontiers Media S.A.
2025-09-01
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| Col·lecció: | Frontiers in Cell and Developmental Biology |
| Matèries: | |
| Accés en línia: | https://www.frontiersin.org/articles/10.3389/fcell.2025.1640275/full |
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