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Stem/progenitor cell-based therapy for Duchenne muscular dystrophy

Duchenne muscular dystrophy is a genetic disease where loss of sarcolemma-associated protein, dystrophin, leads to progressive muscle wasting, and eventual loss of life from complications linked to cardiac deficits. Currently, numerous molecular therapies to restore dystrophin have entered clinical...

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Autors principals: Tsukasa Tominari, Chaitra Sathyaprakash, Yoshitsugu Aoki
Format: Artigo
Idioma:Inglês
Publicat: Frontiers Media S.A. 2025-09-01
Col·lecció:Frontiers in Cell and Developmental Biology
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Accés en línia:https://www.frontiersin.org/articles/10.3389/fcell.2025.1640275/full
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