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Use of Sirolimus and Immunoglobulin Replacement Therapy (IRT) in Patients with Activated Phosphoinositide 3-Kinase Delta Syndrome (APDS): A Systematic Literature Review (SLR)

IntroductionActivated Phosphoinositide 3-Kinase Delta Syndrome (APDS), a rare inborn error of immunity, is associated with immunodeficiency and immune dysregulation. Clinical management includes symptomatic treatment with immunoglobulin replacement therapy (IRT) and sirolimus, neither of which is ap...

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Autori principali: Nicholas L. Hartog, Konrad Pisarczyk, Mike Samad, Katerina Vlachopoulou, Rachel Beckerman, Amanda Harrington
Natura: Artigo
Lingua:Inglês
Pubblicazione: Rockefeller University Press 2026-05-01
Serie:Journal of Human Immunity
Accesso online:https://rupress.org/jhi/article/2/CIS2026/eCIS2026abstract.112/281913/Use-of-Sirolimus-and-Immunoglobulin-Replacement
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