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DISCOVERIES OF GENE EDITING USING CRISPR-CAS9 FOR THE TREATMENT OF SICKLE CELL DISEASE: A LITERATURE REVIEW

Introduction/objectives: Sickle cell disease (SCD) is the most common monogenic blood disorder worldwide, causing reduced life expectancy to the patients. The innovative CRISPR-Cas9 gene-editing technology, pioneered by Jennifer Doudna and Emmanuelle Charpentier, has emerged as a potential curative...

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Xehetasun bibliografikoak
Egile Nagusiak: IS Estevam, CAB Neto, FC Marques, CDC Gentile, EAC Lima, ELF Mota, GF Costa, GS Feitosa, VOC Filho, MM Noronha
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Elsevier 2024-10-01
Saila:Hematology, Transfusion and Cell Therapy
Sarrera elektronikoa:http://www.sciencedirect.com/science/article/pii/S2531137924023253
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