Enhancing hemophilia A gene therapy by strategic F8 deletions in AAV vectors
Hemophilia A, caused by a deficiency in factor VIII (F8), is a promising target for gene therapy. This study aims to enhance the efficacy of adeno-associated virus serotype 8 (AAV8) vectors, specifically those encoding B-domain-deleted F8 (BDDF8), to treat the condition. We focused on improving ther...
में बचाया:
| मुख्य लेखकों: | , , , , , , , , |
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| स्वरूप: | Artigo |
| भाषा: | Inglês |
| प्रकाशित: |
Wolters Kluwer Health
2025-03-01
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| श्रृंखला: | Blood Science |
| ऑनलाइन पहुंच: | http://journals.lww.com/10.1097/BS9.0000000000000217 |
| टैग: |
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