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Micro-utrophin Improves Cardiac and Skeletal Muscle Function of Severely Affected D2/mdx Mice

Duchenne muscular dystrophy (DMD) is an X-linked muscle-wasting disease caused by mutations in the dystrophin gene. DMD boys are wheelchair-bound around 12 years and generally survive into their twenties. There is currently no effective treatment except palliative care, although personalized treatme...

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Главные авторы: Tahnee L. Kennedy, Simon Guiraud, Ben Edwards, Sarah Squire, Lee Moir, Arran Babbs, Guy Odom, Diane Golebiowski, Joel Schneider, Jeffrey S. Chamberlain, Kay E. Davies
Формат: Artigo
Язык:Inglês
Опубликовано: Elsevier 2018-12-01
Серии:Molecular Therapy: Methods & Clinical Development
Online-ссылка:http://www.sciencedirect.com/science/article/pii/S2329050118301013
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