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Therapeutic Application and Structural Features of Adeno-Associated Virus Vector

Adeno-associated virus (AAV) is characterized by non-pathogenicity, long-term infection, and broad tropism and is actively developed as a vector virus for gene therapy products. AAV is classified into more than 100 serotypes based on differences in the amino acid sequence of the capsid protein. Endo...

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Autors principals: Yasunari Matsuzaka, Ryu Yashiro
Format: Artigo
Idioma:Inglês
Publicat: MDPI AG 2024-08-01
Col·lecció:Current Issues in Molecular Biology
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Accés en línia:https://www.mdpi.com/1467-3045/46/8/499
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