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HTRS2025.O8C.4 Efficacy and Safety of Giroctocogene Fitelparvovec in Adults With Moderately Severe to Severe Hemophilia A: Results From the Phase 3 AFFINE Gene Therapy Trial

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書目詳細資料
Principais autores: Caroline Berube, Andrew D. Leavitt, Barbara A. Konkle, Tseng Li-Jung, Danica Chiu, Pascal Klaus, Jasmine Healy, Delphine Agathon, Frank Plonski
格式: Artigo
語言:Inglês
出版: Elsevier 2025-11-01
叢編:Research and Practice in Thrombosis and Haemostasis
在線閱讀:http://www.sciencedirect.com/science/article/pii/S2475037925004807
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