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HTRS2025.O8C.4 Efficacy and Safety of Giroctocogene Fitelparvovec in Adults With Moderately Severe to Severe Hemophilia A: Results From the Phase 3 AFFINE Gene Therapy Trial

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Bibliografiske detaljer
Principais autores: Caroline Berube, Andrew D. Leavitt, Barbara A. Konkle, Tseng Li-Jung, Danica Chiu, Pascal Klaus, Jasmine Healy, Delphine Agathon, Frank Plonski
Format: Artigo
Sprog:Inglês
Udgivet: Elsevier 2025-11-01
Serier:Research and Practice in Thrombosis and Haemostasis
Online adgang:http://www.sciencedirect.com/science/article/pii/S2475037925004807
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