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Long-term progression of clinician-reported and gait performance outcomes in hereditary spastic paraplegias

IntroductionHereditary spastic paraplegias (HSPs) are a heterogeneous group of neurodegenerative diseases in which little is known about the most appropriate clinical outcome assessments (COAs) to capture disease progression. The objective of this study was to prospectively determine disease progres...

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Autors principals: Diana Maria Cubillos Arcila, Gustavo Dariva Machado, Valéria Feijó Martins, Vanessa Bielefeldt Leotti, Rebecca Schüle, Leonardo Alexandre Peyré-Tartaruga, Jonas Alex Morales Saute
Format: Artigo
Idioma:Inglês
Publicat: Frontiers Media S.A. 2023-09-01
Col·lecció:Frontiers in Neuroscience
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Accés en línia:https://www.frontiersin.org/articles/10.3389/fnins.2023.1226479/full
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