QR Code

Rebalancing Hemostasis: Fitusiran as a First‐in‐Class RNAi Therapy in Hemophilia A and B

ABSTRACT Background and Aims Fitusiran is a first‐in‐class RNA interference (RNAi) therapy that lowers antithrombin (AT) to rebalance hemostasis in people with Hemophilia A or B, with or without inhibitors. Its recent FDA approval marks a major shift toward factor‐independent prophylaxis. This comme...

Description complète

Enregistré dans:
Détails bibliographiques
Auteurs principaux: Raza Ur Rehman, Rida Fatima, Aymar Akilimali
Format: Artigo
Langue:Inglês
Publié: Wiley 2026-01-01
Collection:Health Science Reports
Accès en ligne:https://doi.org/10.1002/hsr2.71702
Tags: Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!