Long-term safety and efficacy of fitusiran prophylaxis, and perioperative management, in people with hemophilia A or B

Abstract: Fitusiran is an investigational small interfering RNA therapeutic that targets antithrombin (AT) to rebalance hemostasis in people with hemophilia. Here, we present the results of a completed phase 2 open-label extension study, which evaluated the long-term safety and efficacy of fitusiran...

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Detalhes bibliográficos

Principais autores:	Steven W. Pipe, Toshko Lissitchkov, Pencho Georgiev, Sarah Mangles, Inga Hegemann, Alice Trinchero, Pratima Chowdary, Adam Forbes, Liqi Feng, Laurel A. Menapace, Salim Kichou, Shauna Andersson, Marek Demissie, Margaret V. Ragni
Formato:	Artigo
Idioma:	Inglês
Publicado em:	Elsevier 2025-03-01
coleção:	Blood Advances
Acesso em linha:	http://www.sciencedirect.com/science/article/pii/S2473952924007110
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