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MicroRNA‐based recombinant AAV vector assembly improves efficiency of suicide gene transfer in a murine model of lymphoma

Abstract Recent success in clinical trials with recombinant Adeno‐associated virus (AAV)‐based gene therapy has redirected efforts in optimizing AAV assembly and production, to improve its potency. We reasoned that inclusion of a small RNA during vector assembly, which specifically alters the phosph...

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Principais autores: Nusrat Khan, Sabna Cheemadan, Himanshi Saxena, Sridhar Bammidi, Giridhara R. Jayandharan
Formato: Artigo
Idioma:Inglês
Publicado em: Wiley 2020-05-01
coleção:Cancer Medicine
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Acesso em linha:https://doi.org/10.1002/cam4.2935
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