A prospective short-term study to evaluate methodologies for the assessment of disease extent, impact, and wound evolution in patients with dystrophic epidermolysis bullosa

Abstract Background Standardized assessments for dystrophic epidermolysis bullosa (DEB) are needed. This prospective, multicenter, 4-week, observational study was designed to evaluate DEB assessments for suitability as clinical trial endpoints. Methods Patients with confirmed DEB diagnosis and ≥ 5 m...

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Detalles Bibliográficos

Autores principales:	Amy S. Paller, Elena Pope, Dan Rudin, Anna Malyala, Deborah Ramsdell, Ramsey Johnson, Hal Landy, Dedee F. Murrell, the DEB Investigators
Formato:	Artigo
Lenguaje:	Inglês
Publicado:	BMC 2022-08-01
Colección:	Orphanet Journal of Rare Diseases
Materias:	Dystrophic epidermolysis bullosa Clinician-assessed outcomes Quality of life Patient-reported outcomes Disease severity Outcome measures
Acceso en línea:	https://doi.org/10.1186/s13023-022-02461-z
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