A prospective short-term study to evaluate methodologies for the assessment of disease extent, impact, and wound evolution in patients with dystrophic epidermolysis bullosa

Abstract Background Standardized assessments for dystrophic epidermolysis bullosa (DEB) are needed. This prospective, multicenter, 4-week, observational study was designed to evaluate DEB assessments for suitability as clinical trial endpoints. Methods Patients with confirmed DEB diagnosis and ≥ 5 m...

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Asıl Yazarlar:	Amy S. Paller, Elena Pope, Dan Rudin, Anna Malyala, Deborah Ramsdell, Ramsey Johnson, Hal Landy, Dedee F. Murrell, the DEB Investigators
Materyal Türü:	Artigo
Dil:	Inglês
Baskı/Yayın Bilgisi:	BMC 2022-08-01
Seri Bilgileri:	Orphanet Journal of Rare Diseases
Konular:	Dystrophic epidermolysis bullosa Clinician-assessed outcomes Quality of life Patient-reported outcomes Disease severity Outcome measures
Online Erişim:	https://doi.org/10.1186/s13023-022-02461-z
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