Selection of specific and efficient siRNAs in new cellular model for Hutchinson-Gilford progeria syndrome therapy
Hutchinson-Gilford progeria syndrome is a fatal genetic disorder caused by a point mutation in the gene encoding the nuclear envelope protein lamin A/C. The most frequent mutation leads to the synthesis of a shorter version of lamin A named progerin, which accumulates under the nuclear membrane, lea...
保存先:
| 主要な著者: | , , , |
|---|---|
| フォーマット: | Artigo |
| 言語: | Inglês |
| 出版事項: |
Elsevier
2025-12-01
|
| シリーズ: | Molecular Therapy: Nucleic Acids |
| 主題: | |
| オンライン･アクセス: | http://www.sciencedirect.com/science/article/pii/S2162253125002811 |
| タグ: |
タグなし, このレコードへの初めてのタグを付けませんか!
|