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Thorough molecular configuration analysis of noncanonical AAV genomes in AAV vector preparations

The unique palindromic inverted terminal repeats (ITRs) and single-stranded nature of adeno-associated virus (AAV) DNA are major hurdles to current sequencing technologies. Due to these characteristics, sequencing noncanonical AAV genomes present in AAV vector preparations remains challenging. To ad...

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主要な著者: Junping Zhang, Xiangping Yu, Matthew Chrzanowski, Jiahe Tian, Derek Pouchnik, Ping Guo, Roland W. Herzog, Weidong Xiao
フォーマット: Artigo
言語:Inglês
出版事項: Elsevier 2024-03-01
シリーズ:Molecular Therapy: Methods & Clinical Development
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オンライン・アクセス:http://www.sciencedirect.com/science/article/pii/S2329050124000317
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