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Caffeine boosts Ataluren's readthrough activity

The readthrough of nonsense mutations by small molecules like Ataluren is considered a novel therapeutic approach to overcome the gene defect in several genetic diseases as cystic fibrosis (CF). This pharmacological approach suppresses translation termination at premature termination codons (PTCs re...

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Xehetasun bibliografikoak
Egile Nagusiak: Laura Lentini, Raffaella Melfi, Patrizia Cancemi, Ivana Pibiri, Aldo Di Leonardo
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Elsevier 2019-06-01
Saila:Heliyon
Gaiak:
Sarrera elektronikoa:http://www.sciencedirect.com/science/article/pii/S2405844019355744
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