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Targeted RNA base editing for therapeutic: mechanisms and advances

RNA base editing, which enables RNA base modification through effector proteins guided by targeting systems, is a powerful technology to correct disease-associated point mutations. Although overshadowed by CRISPR-based genome editing, RNA editing has seen rapid development in recent years, with sign...

Ausführliche Beschreibung

Gespeichert in:
Bibliografische Detailangaben
Hauptverfasser: Weikai Yan, Xiaocheng Weng
Format: Artigo
Sprache:Inglês
Veröffentlicht: Elsevier 2025-12-01
Schriftenreihe:Pharmaceutical Science Advances
Schlagworte:
Online-Zugang:http://www.sciencedirect.com/science/article/pii/S2773216925000273
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